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Хвороба фон Віллебранда, тип 3

ORPHA:166096· ICD-10 D68.0· Von Willebrand disease type 3

Визначення(English summary)

A form of von Willebrand disease (VWD) characterized by a bleeding disorder associated with a total or near-total absence of Willebrand factor (VWF) in the plasma and cellular compartments, also leading to a profound deficiency of plasmatic factor VIII (FVIII). It is the most severe form of VWD.

Поширеність
1-9 / 1 000 000
Успадкування
Autosomal recessive
Вік початку
Infancy, Neonatal