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Hypocalcemic vitamin D-dependent rickets

ORPHA:289157· ICD-10 E55.0

Definition

A rare, genetic disorder of vitamin D metabolism characterized by severe hypocalcemia leading to osteomalacia and rachitic bone deformations, and moderate hypophosphatemia.

Prevalence
1-5 / 10 000
Inheritance
Autosomal recessive
Age of onset
Infancy, Neonatal