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点突变所致PURA相关性严重新生儿肌张力低下-癫痫-脑病综合征

ORPHA:438216· ICD-10 G40.4· PURA-related severe neonatal hypotonia-seizures-encephalopathy syndrome due to a point mutation

患病率
<1 / 1 000 000
遗传方式
Autosomal dominant, Not applicable
发病年龄
Infancy, Neonatal