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PCNA-assoziiertes progressives neurodegeneratives photosensitives-Syndrom

ORPHA:438134· ICD-10 G11.3· PCNA-related progressive neurodegenerative photosensitivity syndrome

Prävalenz
<1 / 1 000 000
Vererbung
Autosomal recessive
Erkrankungsalter
Infancy, Neonatal