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Mendelian susceptibility to mycobacterial diseases due to partial STAT1 deficiency

ORPHA:319595· ICD-10 D84.8

Definition

Mendelian susceptibility to mycobacterial diseases (MSMD) due to partial STAT1 (signal transducer and activator of transcription 1) deficiency is a genetic variant of MSMD characterized by a partial defect in the interferon (IFN)-gamma pathway, leading to mild mycobacterial infections.

Prevalence
<1 / 1 000 000
Inheritance
Autosomal dominant
Age of onset
Childhood