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Congenital fiber-type disproportion myopathy

ORPHA:2020· ICD-10 G71.2

Definition

A rare genetic, congenital, non-dystrophic myopathy characterized by neonatal or infantile-onset hypotonia and mild to severe generalized muscle weakness.

Prevalence
Unknown
Inheritance
Autosomal dominant, Autosomal recessive, X-linked recessive
Age of onset
Infancy, Neonatal