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进行性脊椎干骺端发育不全-身材矮小-第四跖骨短-智力障碍综合征

ORPHA:457395· ICD-10 Q87.8· Progressive spondyloepimetaphyseal dysplasia-short stature-short fourth metatarsals-intellectual disability syndrome

患病率
<1 / 1 000 000
遗传方式
Autosomal recessive
发病年龄
Infancy, Neonatal