vitalwiki

EP300单抗不足所致Rubinstein-Taybi综合征

ORPHA:353284· ICD-10 Q87.2· Rubinstein-Taybi syndrome due to EP300 haploinsufficiency

患病率
<1 / 1 000 000
遗传方式
Autosomal dominant
发病年龄
Neonatal