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Дефіцит пуриннуклеозидфосфорилази

ORPHA:760· ICD-10 D81.5· Purine nucleoside phosphorylase deficiency

Визначення(English summary)

A rare immune disease characterized by progressive immunodeficiency leading to recurrent and opportunistic infections, autoimmunity and malignancy as well as neurologic manifestations.

Поширеність
<1 / 1 000 000
Успадкування
Autosomal recessive
Вік початку
Adolescent, Childhood, Infancy