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Синдром Марінеско-Шогрена

ORPHA:559· ICD-10 G11.1· Marinesco-Sjögren syndrome

Визначення(English summary)

A rare autosomal recessive disorder characterized by cerebellar ataxia, early-onset bilateral cataracts, chronic myopathy; additional features are delayed motor development and variable intellectual disability, hypergonadotrophic hypogonadism and delayed puberty, and short stature.

Поширеність
<1 / 1 000 000
Успадкування
Autosomal recessive
Вік початку
Childhood, Infancy