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Гіпофосфатазія

ORPHA:436· ICD-10 E83.3· Hypophosphatasia

Визначення(English summary)

A rare, genetic metabolic disorder characterized by reduced activity of unfractionated serum alkaline phosphatase (ALP) and various symptoms from life-threatening, severely impaired mineralization at birth to musculo-skeletal pain in adulthood.

Поширеність
Unknown
Успадкування
Autosomal dominant, Autosomal recessive
Вік початку
All ages