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Панцитопенія, зумовлена мутацією IKZF1

ORPHA:317473· ICD-10 D81.8· Common variable immunodeficiency phenotype due to IKAROS functional haploinsufficiency

Визначення(English summary)

A rare syndrome with combined immunodeficiency characterized by a variable clinical presentation ranging from asymptomatic individuals to potentially life-threatening, recurrent bacterial infections associated with progressive loss of serum immunoglobulins and B cells.

Поширеність
<1 / 1 000 000
Успадкування
Autosomal dominant
Вік початку
Adolescent, Adult, Childhood, Infancy, Neonatal