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Congenital dyserythropoietic anemia type I

ORPHA:98869· ICD-10 D64.4

Definition

A form of congenital dyserythropoietic anemia (CDA) characterized by moderate to severe anemia, often macrocytic, occasionally associated with congenital malformations, primarily affecting the distal extremities.

Prevalence
<1 / 1 000 000
Inheritance
Autosomal recessive
Age of onset
Adolescent, Adult, Childhood, Infancy, Neonatal