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Hemolytic anemia due to red cell pyruvate kinase deficiency

ORPHA:766· ICD-10 D55.2

Definition

A rare, genetic metabolic disorder due to pyruvate kinase deficiency characterized by a variable degree of chronic nonspherocytic hemolytic anemia resulting in a variable clinical manifestations ranging from fatal anemia at birth to a to a fully compensated hemolysis without apparent anemia.

Prevalence
1-9 / 100 000
Inheritance
Autosomal recessive
Age of onset
Infancy, Neonatal