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GRACILE syndrome

ORPHA:53693· ICD-10 E88.8

Definition

An inherited lethal mitochondrial disorder characterized by fetal growth restriction (GR), aminoaciduria (A), cholestasis (C), iron overload (I), lactacidosis (L), and early death (E).

Prevalence
1-9 / 100 000
Inheritance
Autosomal recessive
Age of onset
Antenatal, Neonatal