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Homocystinuria due to methylene tetrahydrofolate reductase deficiency

ORPHA:395· ICD-10 E72.1

Definition

Homocystinuria due to methylene tetrahydrofolate reductase (MTHFR) deficiency is a metabolic disorder characterised by neurological manifestations.

Prevalence
Unknown
Inheritance
Autosomal recessive
Age of onset
Infancy, Neonatal