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CLN12 disease

ORPHA:314632· ICD-10 E75.4

Definition

A rare neuronal ceroid lipofuscinosis characterized by juvenile-onset (11-13 years) ataxia, unsteady gait, severe myoclonus and mood disturbance, progressing with clear extrapyramidal symptoms (including akinesia, rigidity and dysarthric speech) in 5 years following the diagnosis.

Prevalence
<1 / 1 000 000
Inheritance
Autosomal recessive
Age of onset
Childhood