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Піридоксинзалежна епілепсія

ORPHA:3006· ICD-10 G40.8· Pyridoxine-dependent-developmental and epileptic encephalopathy

Визначення(English summary)

A rare neurometabolic disease characterized by recurrent intractable seizures in the prenatal, neonatal and postnatal period that are resistant to anti-epileptic drugs (AEDs) but that are responsive to pharmacological dosages of pyridoxine (vitamin B6).

Поширеність
Unknown
Успадкування
Autosomal recessive
Вік початку
Antenatal, Infancy, Neonatal