RNU4-2-related autosomal dominant neurodevelopmental disorder
ORPHA:686488
Definition
A rare, genetic, syndromic neurodevelopmental disorder characterized by global development delay with absent/poor speech, mild to profound intellectual disability, hypotonia and microcephaly. Other common clinical manifestations include brain abnormalities, behavioral disturbances, seizures, ophthalmological and skeletal manifestations, feeding difficulties, weight gain problems and distinctive facial features.
- Prevalence
- <1 / 1 000 000
- Inheritance
- Autosomal dominant
- Age of onset
- Antenatal, Neonatal