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X-linked creatine transporter deficiency

ORPHA:52503· ICD-10 E72.8

Definition

X-linked creatine transporter deficiency (CRTR-D) is a creatine deficiency syndrome characterized clinically by global developmental delay/ intellectual disability (DD/ID) with prominent speech/language delay, autistic behavior and seizures.

Prevalence
Unknown
Inheritance
Not applicable, X-linked recessive
Age of onset
Childhood, Infancy