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Adenylosuccinate lyase deficiency

ORPHA:46· ICD-10 E79.8

Definition

A disorder of purine metabolism characterized by intellectual disability, psychomotor delay and/or regression, seizures, and autistic features.

Prevalence
<1 / 1 000 000
Inheritance
Autosomal recessive
Age of onset
Childhood, Infancy, Neonatal