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COASY protein-associated neurodegeneration

ORPHA:397725· ICD-10 G23.0

Definition

COASY protein-associated neurodegeneration (CoPAN) is a very rare, slowly progressive form of neurodegeneration with brain iron accumulation (NBIA) characterized by classic NBIA features. The clinical manifestations include early-onset spastic-dystonic paraparesis, oromandibular dystonia, dysarthria, parkinsonism, axonal neuropathy, progressive cognitive impairment, complex motor tics, and obsessive-compulsive disorder.

Prevalence
<1 / 1 000 000
Inheritance
Autosomal recessive
Age of onset
Childhood