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Short stature due to partial GHR deficiency

ORPHA:314802· ICD-10 E34.3

Definition

Short stature due to partial GHR deficiency is a rare, genetic, endocrine disease characterized by idiopathic short stature due to diminished GHR function (decreased ligand binding or reduced availability of receptor), thus resulting in partial insensitivity to growth hormone.

Prevalence
Unknown
Inheritance
Unknown
Age of onset
Childhood