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X-linked sideroblastic anemia and spinocerebellar ataxia

ORPHA:2802· ICD-10 D64.0

Definition

A rare syndromic, inherited form of sideroblastic anemia characterized by mild to moderate anemia (with hypochromia and microcytosis) and early-onset, non- or slowly progressive spinocerebellar ataxia.

Prevalence
<1 / 1 000 000
Inheritance
X-linked recessive
Age of onset
Childhood, Infancy