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脑白质病-脊柱干骺端发育不良综合征

ORPHA:83629· ICD-10 G37.8· Leukoencephalopathy-spondyloepimetaphyseal dysplasia syndrome

患病率
<1 / 1 000 000
遗传方式
X-linked recessive
发病年龄
Childhood, Infancy