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Fanconi anemia

ORPHA:84· ICD-10 D61.0

Definition

A rare genetic multisystem disorder characterized by progressive pancytopenia with bone marrow failure, variable congenital malformations and predisposition to develop hematological or solid tumors.

Prevalence
1-9 / 100 000
Inheritance
Autosomal recessive, X-linked recessive
Age of onset
Childhood