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Aceruloplasminemia

ORPHA:48818· ICD-10 E83.1

Definition

A rare adult-onset disorder of neurodegeneration with brain iron accumulation (NBIA) characterized by anemia, retinal degeneration, diabetes and various neurological symptoms.

Prevalence
<1 / 1 000 000
Inheritance
Autosomal recessive
Age of onset
Adult, Elderly