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PPARG-related familial partial lipodystrophy

ORPHA:79083· ICD-10 E88.1

Definition

A rare familial partial lipodystrophy characterized by adult onset of distal lipoatrophy with gluteofemoral fat loss, as well as increased fat accumulation in the face and trunk and visceral adiposity. Additional manifestations include diabetes mellitus, atherogenic dyslipidemia, eyelid xanthelasmas, arterial hypertension, cardiovascular disease, hepatic steatosis, acanthosis nigricans on axillae and neck, hirsutism, and muscular hypertrophy of the lower limbs.

Prevalence
<1 / 1 000 000
Inheritance
Autosomal dominant
Age of onset
Adult